UK’s first gene therapy baby celebrates 21st birthday
1 Oct 2021, 11 a.m.
The first child to be treated in the UK with gene therapy celebrates his 21st birthday this week, twenty years after having the pioneering treatment at Great Ormond Street Hospital for Children (GOSH).
Great Ormond Street Hospital for Children (GOSH) and Sensyne have announced a new partnership to improve children’s lives using clinical artificial intelligence to analyse anonymised patient data.
Clinical trial improves outcomes for children on ventilators
24 Aug 2021, noon
Trial finds that a greater involvement of nurses, minimising sedation use and increasing daily testing to assess the child’s readiness to come off the ventilator significantly reduced the time on mechanical ventilation.
Gene therapy offers hope to children with rare and fatal brain diseases
29 Jun 2021, 10 a.m.
Scientists and doctors at UCL GOS ICH and GOSH have given hope of a gene therapy cure to children with a rare degenerative brain disorder called Dopamine Transporter Deficiency Syndrome (DTDS)