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NIHR GOSH BRC spinout Orchard Therapeutics signs strategic agreement with GSK

13 Apr 2018, 1:10 p.m.

GSK and Orchard Therapeutics today announced a strategic agreement, under which GSK will transfer its portfolio of approved and investigational rare disease gene therapies to Orchard, securing the continued development of the programmes and access for pat

Novel therapy for Battens Disease available on the NHS

19 Sep 2019, 4:04 p.m.

Patients at Great Ormond Street Hospital (GOSH) and across England are set to receive treatment for the rare nervous system condition Battens Disease, following a deal between the NHS and manufacturer Biomarin. The drug, which is called cerliponase alfa o

Burosumab treatment for XLH Rickets_before and after

Precision medicine improves growth for children with a rare form of rickets

6 Jul 2018, 10:39 a.m.

A new, targeted drug has been shown to significantly improve growth and control of rickets in children with X-linked hypophosphataemic rickets (XLH), a serious condition affecting about 300 children in the UK.

Rapid DNA sequencing is saving the lives of critically ill children

27 Jul 2018, 9:29 a.m.

A new rapid sequencing technique has helped doctors at Great Ormond Street Hospital (GOSH) to quickly diagnose children in intensive care, enabling them to receive the best treatment and reducing the time they have to spend hospital.

Professor Thomas Voit at the GOSH Biomedical Research Centre showcase

Research successes highlighted at BRC showcase event

16 Apr 2019, 4:27 p.m.

Over 150 people came along to the National Institute for Health Research (NIHR) GOSH Biomedical Research Centre showcase last month to hear about our latest research highlights - from cutting edge CAR-T therapies for leukaemia, to Oculome genomic sequenci

GOSH researchers join experts in warning of the detrimental impact of a no deal Brexit on rare diseases

11 Dec 2020, 4:24 p.m.

Experts have warned that a ‘no deal’ Brexit will result in the exclusion of the UK from the 24 European Reference Networks (ERNs) that were established to improve the care of patients bearing the lifelong burden of a rare disease, which require highly spe

Leukaemia trial shows promise and complexity of genome-edited cell therapies

12 Dec 2020, 5:16 p.m.

A ‘one size fits all’ immune therapy developed at the UCL Great Ormond Street Institute of Child Health (ICH) could help to clear cancerous cells in children and adults who have exhausted all other treatment options for B-cell acute lymphoblastic leukaemi

A selection of images from the 2021 competition

A Moment of Discovery 2022

9 Nov 2022, 3 p.m.

The Research and Innovation Communications team at GOSH/the NIHR GOSH BRC invite you to enter our Research and Innovation Showcase: A Moment of Discovery.

A selection of images from the 2nd annual NIHR GOSH BRC competition

3rd Annual NIHR GOSH BRC Image Competition - A Moment of Discovery

1 Nov 2023, noon

The Research and Innovation Communications team at GOSH and the NIHR GOSH Biomedical Research invite you to enter our Research and Innovation Showcase: A Moment of Discovery.