GOSH researchers receive UCL Business Award

23 Jun 2017, 12:57 p.m.

Professors Bobby Gasper and Adrian Thrasher, both members of the BRC senior management team, have been awarded the UCL Business Award, in recognition of their work on the spin-out company Orchard Therapeutics.

Orchard is a biotechnology company focused on the development and commercialization of gene therapy medicines for children with rare diseases. It was launched in May 2016 with support from UCL Business and a £21 million investment from F-Prime Capital Partners.

Orchard focusses on restoring normal gene function in immunodeficiencies, metabolic diseases and haematological disorders and builds on GOSH researchers' expertise in stem, cell and gene therapies. Read more.

Professor Gaspar is Deputy Director of the NIHR GOSH BRC and Professor Thrasher is BRC Theme Lead for Gene, Stem and Cellular Therapies.

Reflecting on rare disease day 2025

Rare Disease Day is an international event which takes place annually on the last day of February. The date is chosen because in leap years it is February 29, the rarest date!

Genomics will revolutionise treatment for childhood rare diseases

A global study has proven the power of a simple genomics blood test to improve treatment and care for childhood epilepsy.

Predicting how childhood kidney cancers develop

New research has analysed how the childhood kidney cancer, Wilms tumour, evolves in children who are more at risk from developing the cancer.

Join us in the countdown to Rare Disease Day 2025

Rare Disease Day takes place annually on the last day of February and is a global opportunity to increase awareness and advocate for those living with rare conditions.