Genetic sequencing improved the diagnosis of abnormalities detected in ultrasound scans of developing babies, in new research from Great Ormond Street Hospital (GOSH), the Wellcome Sanger Institute and Birmingham Women’s Hospital.
A new, targeted treatment for the rare form of rickets called X-Linked Hypophosphataemia (XLH) is now available to NHS patients from 8 January 2019, following an international clinical trial.
Researchers at Great Ormond Street Hospital (GOSH) and the UCL Great Ormond Street Institute of Child Health (ICH) are to lead a new collaboration exploring how stem cells can be engineered to evade immune responses.
Clinical trials of a pioneering new cancer therapy known as AUTO3, developed by UCL spinout company Autolus Therapeutics, have shown positive initial results.
Paediatric researchers from across the UK came together for a special training weekend hosted by the NIHR GOSH Biomedical Research Centre (BRC) earlier this month.