https://www.gosh.nhs.uk/our-research/our-research-infrastructure/nihr-great-ormond-street-hospital-brc/brc-news/?page=40

Biomedical Research Centre news

£75,000 boost for Duchenne Muscular Dystrophy gene therapy research

8 Aug 2017, 4:03 p.m.

GOSH Biomedical Research Centre researcher Dr John Counsell has been awarded up to £75,000 of funding from the UCL Therapeutic Acceleration Support (TAS) Fund for a study exploring the use of novel vectors in gene therapy for Duchenne Muscular Dystrophy (

GOSH researchers receive UCL Business Award

23 Jun 2017, 12:57 p.m.

Professors Bobby Gasper and Adrian Thrasher, both members of the BRC senior management team, have been awarded the UCL Business Award, in recognition of their work on the spin-out company Orchard Therapeutics.

Cannabidiol trial shows reduction in seizures for children with Dravet syndrome

30 May 2017, 12:58 p.m.

A trial conducted in Europe and the USA has shown that cannabidiol – a drug derived from cannabis but with the psycho-active elements removed – reduces seizures in children with a form of drug resistant epilepsy, known as Dravet syndrome.

Molecular diagnoses of century-old childhood tumours reveals cancer causing mutations

24 May 2017, 2:29 p.m.

A collection of 100-year old tumour samples held at Great Ormond Street Hospital (GOSH) has helped pinpoint the genetic mutations that cause some of the rarest childhood cancers.

Researchers announce oesophagus regeneration trial

24 Apr 2017, 3 p.m.

A team led by Professor Paolo De Coppi has announced that they are set to build and transplant an oesophagus using organs harvested from pigs and then modified using a child’s stem cells. The organs will be created for children who are born with a severe