Steps forward in gene therapy for hearing loss linked to rare disease
29 Aug 2023, 3 p.m.
An international team led by researchers at GOSH, UCL and the NIHR GOSH BRC have developed in mice a gene therapy that significantly reduces the hearing loss associated with Norrie disease.
Global genomic collaboration improves lives and treatment for children with epilepsy
17 Aug 2023, 8 a.m.
An international research collaboration, including GOSH and our research partner UCL Institute of Child Health, has shown that a technique known as rapid genome sequencing can provide a diagnosis for 43 per cent of children with unexplained epilepsy.
Unlocking the mystery of long-lasting cancer treatment
6 Jul 2023, 8 a.m.
Researchers from across GOSH, UCL GOS ICH and the Wellcome Sanger Institute have published new insights that explain why some children have a longer remission than others after having cutting-edge CAR T-cell therapy for leukaemia.